Gene therapy for rare form of autism may treat another
A MECP2 gene therapy for Rett syndrome eases repetitive behaviors, anxiety and hyperactivity in a mouse model of Pitt-Hopkins syndrome.
Efforts to ease the symptoms of autism are beginning to ramp up, with promising candidates in various stages of testing.
A MECP2 gene therapy for Rett syndrome eases repetitive behaviors, anxiety and hyperactivity in a mouse model of Pitt-Hopkins syndrome.
These short reports from Spectrum journalists highlight some of the autism-related findings that caught our attention at the meeting this past week.
Cannabis-derived drugs are approved to treat only a small number of autism-related conditions, but many autistic people and their families experiment with medical marijuana to ease autism traits. In this special report, Spectrum rounds up what the science says about cannabis and autism.
Dysfunctional circuits and a rogue sodium channel in the brainstem may explain the disordered breathing pattern seen in children with Pitt-Hopkins syndrome, a form of autism.
The possibility of microbial treatments for autism has inspired a burst of research and nascent clinical trials, but new research suggests these efforts rest on shaky scientific ground.
The hormone is no better than placebo at boosting social behavior in autistic children, according to a new study, but it may still benefit a subset of people with the condition.
After imposing a pause in November 2020, the U.S. Food and Drug Administration has cleared the way for a clinical trial of a gene therapy for Angelman syndrome.
A drug that helps promote gene expression reduces repetitive behaviors and improves memory and sociability in a mouse model of autism.
Preliminary results suggested the treatment is no better than placebo at reducing the severity of core autism traits.
Experts question data showing that an experimental therapy that parents deliver to babies with early signs of autism can lessen the intensity of the children’s traits and lower their chances of diagnosis at age 3.